Official Title
Expanded Access Treatment with LP352 for Patients with Developmental and Epileptic Encephalopathies (DEEs) Who Successfully Completed an LP352 Clinical Trial (Intermediate-Size EAP)
Brief Summary

This is an intermediate-size expanded access program (EAP) study. The purpose of this EAPis to provide continued access to LP352, an investigational drug product beinginvestigated in participants with DEEs. The EAP study will allow continued treatment withLP352 for eligible participants diagnosed with treatment resistant DEEs who successfullycompleted an LP352 Clinical Trial (Enrollment by Invitation) or an immediate familymember who has the exact same gene mutation resulting in the same DEE epilepsy syndromephenotype or a patient who previously participated in the lorcaserin EAP.

Detailed Description

Not Provided

Available
Intermediate-size Population
Dravet Syndrome
Lennox Gastaut Syndrome
Developmental and Epileptic Encephalopathies

Drug: LP352

LP352 will be administered as a liquid either orally or through a G-tube or Percutaneous
Endoscopic Gastrotomy (PEG) tube.

Eligibility Criteria

Inclusion Criteria:

1. Participant and/or participant's legally authorized representative is willing and
able to provide a written informed consent or assent form before participation in
this EAP. An assent should be obtained from the patient, if possible. Assent must be
obtained for adolescent EAP patients (<18 years of age) as required by local
regulations.

2. Participant with DEE who has successfully completed an LP352 Clinical Trial.

3. Participant currently has clinical benefit from LP352 treatment, as assessed by
their Treating Physician.

4. Participant currently tolerates LP352 treatment and has no safety issue which would
prevent continued treatment.

Exclusion Criteria:

1. Participant was discontinued from an LP352 Clinical Trial for any reason.

2. Any serious and/or unstable new medical condition, psychiatric disorder, or other
conditions at the time of transition to this EAP that could interfere with patient's
safety, obtaining informed consent, assent, or compliance to this EAP protocol, in
the opinion of the Treating Physician.

Eligibility Gender
All
Eligibility Age
Minimum: 2 Years ~ Maximum: 65 Years
Countries
Australia
United States
Locations

Rancho Research Institute
Downey, California, United States

University of California Los Angeles (UCLA)
Los Angeles, California, United States

University of California Benioff Childrens Hospital
San Francisco, California, United States

Colorados Childrens Hospital
Aurora, Colorado, United States

Northwest Florida Clinical Research Group
Gulf Breeze, Florida, United States

Research Institute of Orlando
Orlando, Florida, United States

University of Southern Florida
Tampa, Florida, United States

Hawaii Pacific Neuroscience
Honolulu, Hawaii, United States

Northwestern Medicine Feinberg School of Medicine
Chicago, Illinois, United States

Mid-Atlantic Epilepsy and Sleep Center
Bethesda, Maryland, United States

Corewell Health
Grand Rapids, Michigan, United States

Washington University School of Medicine
Saint Louis, Missouri, United States

New York University (NYU)
New York, New York, United States

Lenox Hill Hospital
New York, New York, United States

University Hospitals Cleveland Medical Center
Cleveland, Ohio, United States

Providence Brain & Spine
Portland, Oregon, United States

Thomas Jefferson University
Philadelphia, Pennsylvania, United States

Children's Neuro Consultants of Austin
Austin, Texas, United States

University of Utah
Salt Lake City, Utah, United States

Austin Hospital, Heidelberg
Heidelberg, Melbourne, Australia

Children's Health Queensland Hospital and Health Service,
South Brisbane, Queensland, Australia

Alfred Hospital
Melbourne, Australia

Contacts

Longboard Study Contact
858-999-8858
clinicalstudies@longboardpharma.com

Not Provided

Longboard Pharmaceuticals
NCT Number
Keywords
CDKL5 deficiency disorder
developmental and epileptic encephalopathy
Dravet Syndrome
Epilepsy
Lennox Gastaut Syndrome
treatment resistant epilepsy
tuberous sclerosis complex
MeSH Terms
Brain Diseases
Epilepsy
Epilepsies, Myoclonic
Lennox Gastaut Syndrome
Syndrome