Officials with the Food and Drug Administration (FDA) recently joined scientists at a public meeting on next steps for conducting research to develop psychedelic medicines.
We, as a society, are past the point of vaping being a new trend. It is now an epidemic for our young people with unfortunately no end in sight if we don’t take action now.
What: The Reagan-Udall Foundation for the FDA will host a public workshop to explore primary disease activity biomarkers in rare genetic diseases. Attendees will hear perspectives from patient advocates, researchers, regulators, and representatives from regulated industry. The discussions will include a series of case studies (heparan sulfate in neuronopathic lysosomal storage diseases) and a dialogue on the challenges in qualifying biomarkers to support rare disease approvals.
